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CLINICAL_TRIALS trial_result · 2025-02-19

Clinical Trial Update: Open-label, Pivotal Clinical Trial to Confirm Efficacy and Safety of Autologous Grafts Containing Stem Cells Genetically Modified for Epidermis Restoration in Patients With Junctional Epidermolysis Bullosa [Phase 2, Phase 3]

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Summary

An open-label pivotal trial of autologous, gene-modified stem cell grafts for epidermis restoration in Junctional Epidermolysis Bullosa has been terminated.

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Diseases / indications

Drugs mentioned

  • Autologous grafts containing stem cells genetically modified for epidermis restoration

Snippet

Sponsor: Holostem s.r.l. | Conditions: Junctional Epidermolysis Bullosa Non-Herlitz Type | Phase 2, Phase 3 | Status: TERMINATED