Clinical Trial Update: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. [Phase 2]

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Summary

An extension study to assess safety and efficacy in pediatric MPS IIIA patients who participated in a prior study (Phase 2; terminated).

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Diseases / indications

• Mucopolysaccharidosis Type Iiia
• Sanfilippo Syndrome

Drugs mentioned

• Shire

Snippet

Sponsor: Shire | Conditions: Sanfilippo Syndrome, Mucopolysaccharidosis (MPS) | Phase 2 | Status: TERMINATED | Results posted: 2020-04-20