Clinical Trial Update: Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA) [Phase 1, Phase 2]

View source ↗

Summary

Extension study of rhHNS in Sanfilippo Syndrome Type A (MPS IIIA) in Phase 1/2; trial terminated with results posted.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Mucopolysaccharidosis Type Iiia
• Sanfilippo Syndrome Type

Drugs mentioned

• rhHNS (recombinant human iduronidase? (Note: rhHNS refers to a recombinant human heparan/N-sulfoglucosaminidase surrogate; if specific generic name is not provided, set as null))

Snippet

Sponsor: Shire | Conditions: Sanfilippo Syndrome | Phase 1, Phase 2 | Status: TERMINATED | Results posted: 2020-04-21