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CLINICAL_TRIALS trial_result · 2010-09-10

Clinical Trial Update: A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease [Phase 3]

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Summary

Phase 3 trial of GA-GCB enzyme replacement therapy for Gaucher disease type 1 has completed with posted results.

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Diseases / indications

Drugs mentioned

  • Gene-Activated® Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy (glucocerebrosidase)

Snippet

Sponsor: Shire | Conditions: Gaucher Disease, Type 1 | Phase 3 | Status: COMPLETED | Results posted: 2010-09-10