CLINICAL_TRIALS
trial_result
· 2021-08-10
Clinical Trial Update: Safety and Efficacy of Intravenous Trappsol Cyclo (HPBCD) in Niemann-Pick Type C Patients [Phase 1, Phase 2]
Summary
A completed Phase 1/2 clinical trial evaluating intravenous Trappsol Cyclo (HPBCD) for Niemann-Pick disease type C1, focusing on safety and efficacy.
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Snippet
Sponsor: Cyclo Therapeutics, Inc. | Conditions: Niemann-Pick Disease, Type C1 | Phase 1, Phase 2 | Status: COMPLETED