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CLINICAL_TRIALS trial_result · 2021-08-10

Clinical Trial Update: Safety and Efficacy of Intravenous Trappsol Cyclo (HPBCD) in Niemann-Pick Type C Patients [Phase 1, Phase 2]

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Summary

A completed Phase 1/2 clinical trial evaluating intravenous Trappsol Cyclo (HPBCD) for Niemann-Pick disease type C1, focusing on safety and efficacy.

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Diseases / indications

Drugs mentioned

  • Trappsol Cyclo (Hydroxypropyl-β-cyclodextrin)

Snippet

Sponsor: Cyclo Therapeutics, Inc. | Conditions: Niemann-Pick Disease, Type C1 | Phase 1, Phase 2 | Status: COMPLETED