CLINICAL_TRIALS
trial_result
· 2020-08-31
Clinical Trial Update: AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis [Phase 1, Phase 2]
Summary
Clinical trial update on AAVRh.10 administration in children with Late Infantile Neuronal Ceroid Lipofuscinosis (Batten disease) spanning Phase 1 and Phase 2, s…
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Weill Medical College of Cornell University | Conditions: Late Infantile Neuronal Ceroid Lipofuscinosis, Batten Disease | Phase 1, Phase 2 | Status: COMPLETED