Clinical Trial Update: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome [Phase 2]

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Summary

Phase 2 clinical trial assessing safety and efficacy of EPI-743 in children with Leigh Syndrome has been completed.

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Diseases / indications

• Leigh Syndrome

Drugs mentioned

• EPI-743

Snippet

Sponsor: PTC Therapeutics | Conditions: Leigh Syndrome | Phase 2 | Status: COMPLETED