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CLINICAL_TRIALS trial_result · 2020-10-29

Clinical Trial Update: Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD) [Phase 2]

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Summary

Phase 2a extension study of ataluren (PTC124) in Duchenne Muscular Dystrophy was terminated; results posted in 2020.

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Diseases / indications

Drugs mentioned

  • ataluren (ataluren)

Snippet

Sponsor: PTC Therapeutics | Conditions: Duchenne Muscular Dystrophy | Phase 2 | Status: TERMINATED | Results posted: 2020-10-29