Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2025-02-28

Clinical Trial Update: A Randomised Controlled Trial, Of N-Acetyl Cysteine (NAC), for Premanifest Huntingtin Gene Expansion Carriers [Phase 2]

View source ↗

Summary

A Phase 2 randomized trial evaluating N-Acetyl Cysteine (NAC) in premanifest Huntington's disease gene expansion carriers; recruitment is ongoing.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • N-Acetyl-Cysteine (N-acetylcysteine)

Snippet

Sponsor: Western Sydney Local Health District | Conditions: Huntington Disease | Phase 2 | Status: RECRUITING