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CLINICAL_TRIALS trial_result · 2021-01-11

Clinical Trial Update: Pilot Study to Assess Safety, Preliminary Efficacy and Pharmacokinetics of S.C. Pegcetacoplan (APL-2) in PNH Subjects. [Phase 1]

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Summary

Pilot Phase 1 trial evaluating safety, preliminary efficacy, and pharmacokinetics of subcutaneous pegylated complement inhibitor pegcetacoplan (APL-2) in paroxy…

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Diseases / indications

Drugs mentioned

  • Pegcetacoplan (Pegcetacoplan)

Snippet

Sponsor: Apellis Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 1 | Status: COMPLETED | Results posted: 2021-01-11