CLINICAL_TRIALS
trial_result
· 2020-07-07
Clinical Trial Update: Ataluren for Nonsense Mutation Methylmalonic Acidemia [Phase 2]
Summary
Phase 2 clinical trial of ataluren for nonsense mutation-induced methylmalonic acidemia has been terminated; results posted.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: PTC Therapeutics | Conditions: Amino Acid Metabolism, Inborn Errors | Phase 2 | Status: TERMINATED | Results posted: 2020-07-07