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CLINICAL_TRIALS trial_result · 2020-07-15

Clinical Trial Update: Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) [Phase 2]

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Summary

Phase 2B extension study of ataluren in Duchenne/Becker muscular dystrophy was terminated; results posted in 2020.

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Diseases / indications

Drugs mentioned

  • ataluren (ataluren)

Snippet

Sponsor: PTC Therapeutics | Conditions: Duchenne Muscular Dystrophy, Becker Muscular Dystrophy | Phase 2 | Status: TERMINATED | Results posted: 2020-07-15