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CLINICAL_TRIALS research · 2017-12-06

Clinical Trial Update: Sirolimus for Autoimmune Disease of Blood Cells [Phase 1, Phase 2]

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Summary

A phase 1/2 trial evaluating sirolimus for autoimmune blood cell disorders, including autoimmune pancytopenia and ALPS; the study is completed with results post…

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Diseases / indications

Drugs mentioned

  • Sirolimus (Sirolimus)

Snippet

Sponsor: Children's Hospital of Philadelphia | Conditions: Autoimmune Pancytopenia, Autoimmune Lymphoproliferative Syndrome (ALPS) | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2017-12-06