Clinical Trial Update: Dose-Finding Study to Evaluate the Safety, Efficacy, & Tolerability of Multiple Doses of rAvPAL-PEG in Subjects With PKU [Phase 2]

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Summary

Phase 2 dose-finding trial evaluating safety, efficacy, and tolerability of multiple doses of rAvPAL-PEG in phenylketonuria. Results posted after completion.

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Diseases / indications

• Phenylketonuria

Drugs mentioned

• rAvPAL-PEG (recombinant phenylalanine ammonia-lyase enzyme PEGylated)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Phenylketonuria | Phase 2 | Status: COMPLETED | Results posted: 2019-02-26