Clinical Trial Update: Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients with GM2 Gangliosidosis or Niemann-Pick Type C Disease [Phase 2]

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Summary

Phase 2 study evaluating safety, tolerability, pharmacokinetics and pharmacodynamics of oral AZ-3102 in GM2 gangliosidosis and Niemann-Pick disease type C; the …

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Diseases / indications

• Gm2 Gangliosidosis
• Niemann-pick Disease Type

Drugs mentioned

• AZ-3102

Snippet

Sponsor: Azafaros A.G. | Conditions: GM2 Gangliosidosis, Niemann-Pick Disease, Type C | Phase 2 | Status: ACTIVE_NOT_RECRUITING