Clinical Trial Update: Long-term Efficacy of Carglumic Acid in Organic Acidemia. [NA]

View source ↗

Summary

A completed study assessing the long-term efficacy of carglumic acid in organic acidemias. The conditions include Propionic Acidemia and Methylmalonic Acidemia.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Methylmalonic Acidemia
• Propionic Acidemia

Drugs mentioned

• Carglumic acid (Carbaglu) (carglumic acid)

Snippet

Sponsor: National Taiwan University Hospital | Conditions: Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) | NA | Status: COMPLETED