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CLINICAL_TRIALS trial_result · 2019-04-25

Clinical Trial Update: Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia [Phase 3]

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Summary

Phase 3 trial update for Carglumic Acid in Propionic Acidemia and Methylmalonic Acidemia has completed.

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Diseases / indications

Drugs mentioned

  • CARGLUMIC ACID (carglumic acid)

Snippet

Sponsor: King Abdullah International Medical Research Center | Conditions: Propionic Acidemia, Methylmalonic Acidemia | Phase 3 | Status: COMPLETED