Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2025-03-24

Clinical Trial Update: Preparation of IPSC for Cell Gene Editing for the Treatment of AATD [NA]

View source ↗

Summary

This clinical trial update describes preparing induced pluripotent stem cells for gene editing to treat Alpha-1 antitrypsin deficiency, with enrollment by invit…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: Fondazione IRCCS Policlinico San Matteo di Pavia | Conditions: Alpha1-antitrypsin Deficiency | NA | Status: ENROLLING_BY_INVITATION