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CLINICAL_TRIALS trial_result · 2023-11-28

Clinical Trial Update: Single-Arm Study To Evaluate The Efficacy and Safety of Valoctocogene Roxaparvovec in Hemophilia A Patients (BMN 270-301) [Phase 3]

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Summary

Phase 3, single-arm trial evaluating valoctocogene roxaparvovec for Hemophilia A has completed, with results posted on 2023-11-28.

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Diseases / indications

Drugs mentioned

  • Roctavian (valoctocogene roxaparvovec)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Hemophilia A | Phase 3 | Status: COMPLETED | Results posted: 2023-11-28