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CLINICAL_TRIALS research · 2025-03-30

Clinical Trial Update: German Observational Multicenter Study of Patients With Fabry Disease Under Enzyme Replacement Therapy With Pegunigalsidase-alfa

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Summary

This clinical trial update describes an observational multicenter study in Germany evaluating patients with Fabry disease who are receiving enzyme replacement t…

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Diseases / indications

Drugs mentioned

  • Pegunigalsidase alfa (pegunigalsidase alfa)

Snippet

Sponsor: Universität Münster | Conditions: Fabry Disease | Status: RECRUITING