Clinical Trial Update: Safety and Efficacy of Miglustat in Chinese NPC Patients [Phase 4]

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Summary

Phase 4 study in Chinese Niemann-Pick Disease Type C patients evaluated miglustat for safety and efficacy. The trial has completed.

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Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• Miglustat (miglustat)

Snippet

Sponsor: Actelion | Conditions: Niemann-Pick Disease, Type C | Phase 4 | Status: COMPLETED