CLINICAL_TRIALS
trial_result
· 2025-03-30
Clinical Trial Update: A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia [Phase 1]
Summary
A Phase 1 safety and efficacy study evaluating ET-01 for transfusion-dependent beta-thalassemia was terminated.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: EdiGene (GuangZhou) Inc. | Conditions: Transfusion Dependent Beta-Thalassaemia | Phase 1 | Status: TERMINATED