Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2025-03-30

Clinical Trial Update: A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia [Phase 1]

View source ↗

Summary

A Phase 1 safety and efficacy study evaluating ET-01 for transfusion-dependent beta-thalassemia was terminated.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • ET-01

Snippet

Sponsor: EdiGene (GuangZhou) Inc. | Conditions: Transfusion Dependent Beta-Thalassaemia | Phase 1 | Status: TERMINATED