Clinical Trial Update: GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History Study to Assess GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)

View source ↗

Summary

This clinical trial update describes Ultragenyx's GNE-Myopathy Disease Monitoring Program, a registry and prospective natural history study. It assesses GNE myo…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Gne Myopathy
• Hereditary Inclusion Body Myopathy

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Hereditary Inclusion Body Myopathy, GNE Myopathy | Status: COMPLETED