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CLINICAL_TRIALS trial_result · 2017-10-20

Clinical Trial Update: Treatment of the Cholesterol Defect in Smith-Lemli-Opitz Syndrome [Phase 1, Phase 2]

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Summary

Phase 1/2 clinical trial investigating treatment of the cholesterol defect in Smith-Lemli-Opitz Syndrome; status completed with results posted.

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Diseases / indications

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Sponsor: Boston Children's Hospital | Conditions: Smith-Lemli-Opitz Syndrome | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2017-10-20