Clinical Trial Update: Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism [Phase 2]

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Summary

Phase 2 trial update on hematopoietic stem cell transplantation for inborn errors of metabolism; trial terminated with results posted in 2011.

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Diseases / indications

• Hurler Syndrome
• Maroteaux-lamy Syndrome

Snippet

Sponsor: Masonic Cancer Center, University of Minnesota | Conditions: Hurler's Syndrome, Maroteaux-Lamy Syndrome | Phase 2 | Status: TERMINATED | Results posted: 2011-07-13