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CLINICAL_TRIALS trial_result · 2016-04-08

Clinical Trial Update: Phase 1/2 Safety and Efficacy Study of AAV-RPE65 Vector to Treat Leber Congenital Amaurosis [Phase 1, Phase 2]

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Summary

Phase 1/2 study of an AAV-RPE65 gene therapy for Leber congenital amaurosis completed, with results posted in 2016.

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Diseases / indications

Drugs mentioned

  • AAV-RPE65 vector (AAV-RPE65 gene therapy)

Snippet

Sponsor: Beacon Therapeutics | Conditions: Leber Congenital Amaurosis | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2016-04-08