Clinical Trial Update: Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia [Phase 2]

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Summary

Phase 2 trial examining long-term outcomes of N-Carbamylglutamate in Propionic Acidemia and Methylmalonic Acidemia; the study was terminated but results were po…

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Diseases / indications

• Methylmalonic Acidemia
• Propionic Acidemia

Drugs mentioned

• N-Carbamylglutamate (N-carbamylglutamate)

Snippet

Sponsor: Mendel Tuchman | Conditions: Propionic Acidemia, Methylmalonic Acidemia | Phase 2 | Status: TERMINATED | Results posted: 2017-04-26