Clinical Trial Update: Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease

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Summary

This completed clinical trial update investigates using cardiopulmonary exercise testing to quantify the response to enzyme replacement therapy in pediatric Pom…

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Diseases / indications

• Glycogen Storage Disease Type Ii
• Pompe Disease

Drugs mentioned

• LUMIZYME (ALGLUCOSIDASE ALFA)
• Myozyme (alglucosidase alfa)

Snippet

Sponsor: Rambam Health Care Campus | Conditions: Enzyme Replacement Therapy in Pompe Disease | Status: COMPLETED