CLINICAL_TRIALS
trial_result
· 2017-06-23
Clinical Trial Update: Bone Marrow Cell Gene Transfer in Individuals With Fanconi Anemia [Phase 1]
Summary
Phase 1 trial evaluating bone marrow cell gene transfer in individuals with Fanconi Anemia. The study status is completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Boston Children's Hospital | Conditions: Fanconi Anemia | Phase 1 | Status: COMPLETED