Clinical Trial Update: Gene Therapy for the Treatment of Fanconi's Anemia Type C [Phase 1]

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Summary

A Phase 1 gene therapy trial for Fanconi anemia (Type C) has completed. The study addressed pancytopenia associated with the condition.

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Diseases / indications

• Fanconi Anemia
• Pancytopenia

Snippet

Sponsor: National Heart, Lung, and Blood Institute (NHLBI) | Conditions: Fanconi's Anemia, Pancytopenia | Phase 1 | Status: COMPLETED