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CLINICAL_TRIALS approval · 2017-07-24

Clinical Trial Update: A Multicenter, Multi-national Open-label Program to Provide BMN 190 to Patients Diagnosed With CLN2 Disease

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Summary

Marketing approval granted for BioMarin's BMN 190 (cerliponase alfa) to treat CLN2 disease; the therapy is now approved for marketing.

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Diseases / indications

Drugs mentioned

  • BRINEURA (cerliponase alfa)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: CLN2 Disease | Status: APPROVED_FOR_MARKETING