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CLINICAL_TRIALS research · 2025-04-15

Clinical Trial Update: An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics

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Summary

An observational study update evaluating Carbaglu (carglumic acid) for the treatment of hyperammonemia in adults and children with methylmalonic acidemia and pr…

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Diseases / indications

Drugs mentioned

  • Carbaglu (carglumic acid)

Snippet

Sponsor: RECORDATI GROUP | Conditions: Hyperammonemia, Methylmalonic Acidemia | Status: RECRUITING