Clinical Trial Update: A Prospective, Noninterventional, Observational Study of Late-Onset Pompe Disease

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Summary

This is an update on a prospective, noninterventional observational study of late-onset Pompe disease sponsored by BioMarin; the study evaluating patients untre…

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Diseases / indications

• Late-onset Pompe Disease

Drugs mentioned

• Alglucosidase alfa (alglucosidase alfa)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Late-onset Pompe Patients Untreated or Treated With rhGAA | Status: TERMINATED