Clinical Trial Update: Study To Assess Safety, Tolerability and Efficacy of Intravenous Cabaletta in Patients With Machado-Joseph Disease [Phase 2]

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Summary

Phase 2 clinical trial evaluating intravenous Cabaletta for safety, tolerability, and efficacy in Machado-Joseph disease (spinocerebellar ataxia type 3); study …

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Diseases / indications

• Machado-joseph Disease
• Spinocerebellar Ataxia Type 3

Drugs mentioned

• Cabaletta

Snippet

Sponsor: Bioblast Pharma Ltd. | Conditions: Machado-Joseph Disease / Spinocerebellar Ataxia 3 | Phase 2 | Status: COMPLETED