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CLINICAL_TRIALS trial_result · 2025-04-18

Clinical Trial Update: Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

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Summary

This clinical trial update presents long-term follow-up data from subjects treated with voretigene neparvovec-rzyl (AAV2-hRPE65v2) for inherited retinal dystrop…

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Diseases / indications

Drugs mentioned

  • Luxturna (voretigene neparvovec-rzyl)

Snippet

Sponsor: Spark Therapeutics, Inc. | Conditions: Inherited Retinal Dystrophy Due to RPE65 Mutations | Status: ACTIVE_NOT_RECRUITING