CLINICAL_TRIALS
trial_result
· 2025-04-18
Clinical Trial Update: Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
Summary
This clinical trial update presents long-term follow-up data from subjects treated with voretigene neparvovec-rzyl (AAV2-hRPE65v2) for inherited retinal dystrop…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Spark Therapeutics, Inc. | Conditions: Inherited Retinal Dystrophy Due to RPE65 Mutations | Status: ACTIVE_NOT_RECRUITING