Clinical Trial Update: Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping

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Summary

This clinical trial update describes an observational study of Duchenne Muscular Dystrophy patients who could theoretically be treated with exon 53 skipping.

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Diseases / indications

• Duchenne Muscular Dystrophy

Snippet

Sponsor: Genethon | Conditions: Duchenne Muscular Dystrophy | Status: UNKNOWN