Clinical Trial Update: An Expanded Access Protocol for Sebelipase Alfa for Patients With Lysosomal Acid Lipase Deficiency

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Summary

Expanded access protocol for sebelipase alfa to treat lysosomal acid lipase deficiency; the protocol is no longer available.

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Diseases / indications

• Lysosomal Acid Lipase Deficiency

Drugs mentioned

• KANUMA (Sebelipase alfa)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Lysosomal Acid Lipase Deficiency | Status: NO_LONGER_AVAILABLE