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CLINICAL_TRIALS trial_result · 2016-06-27

Clinical Trial Update: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging

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Summary

A completed clinical study used multimodal MRI to assess blood-brain barrier integrity and brain structure in patients with Mucopolysaccharidosis type IIIB (San…

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Diseases / indications

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: MPS IIIB (Sanfilippo B Syndrome) | Status: COMPLETED