Clinical Trial Update: A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype

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Summary

A completed retrospective natural history study of patients with Lysosomal acid lipase deficiency and Wolman disease, documenting clinical features and disease …

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Diseases / indications

• Lysosomal Acid Lipase Deficiency
• Wolman Disease

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Lysosomal Acid Lipase Deficiency, Wolman Disease | Status: COMPLETED