Clinical Trial Update: An Observational Study of Patients With Lysosomal Acid Lipase Deficiency/Cholesteryl Ester Storage Disease Phenotype

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Summary

An observational study of patients with lysosomal acid lipase deficiency and the cholesteryl ester storage disease phenotype has completed.

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Diseases / indications

• Cholesterol Ester Storage Disease
• Lysosomal Acid Lipase Deficiency

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Cholesterol Ester Storage Disease(CESD), Lysosomal Acid Lipase Deficiency | Status: COMPLETED