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CLINICAL_TRIALS trial_result · 2015-11-16

Clinical Trial Update: Natural History Studies of Mucopolysaccharidosis III

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Summary

The document reports the completion of natural history studies for Mucopolysaccharidosis Type IIIA and Type IIIB, sponsored by Nationwide Children's Hospital. T…

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Diseases / indications

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Sponsor: Nationwide Children's Hospital | Conditions: Mucopolysaccharidosis Type IIIA, Mucopolysaccharidosis Type IIIB | Status: COMPLETED