Clinical Trial Update: Sulfamethoxazole for the Treatment of Primary PREPL Deficiency [Phase 2]

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Summary

Phase 2 clinical trial update evaluating sulfamethoxazole for treating primary PREPL deficiency, noted alongside related conditions Hypotonia-Cystinuria Syndrom…

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Diseases / indications

• Hypotonia-cystinuria Syndrome
• Isolated Prepl Deficiency
• Prepl Deficiency

Drugs mentioned

• Sulfamethoxazole (sulfamethoxazole)

Snippet

Sponsor: Universitair Ziekenhuis Brussel | Conditions: Hypotonia Cystinuria Syndrome, Isolated PREPL Deficiency | Phase 2 | Status: UNKNOWN