Clinical Trial Update: Screening Protocol to Evaluate Acid Alpha-Glucosidase (GAA) Activity and GAA Gene Mutations in Patients With Late Onset Pompe Disease

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Summary

This completed clinical trial outlines a screening protocol to measure acid alpha-glucosidase activity and GAA gene mutations in patients with late-onset Pompe …

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Diseases / indications

• Pompe Disease

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Pompe Disease | Status: COMPLETED