Clinical Trial Update: Wolman/CESD Natural History Chart Review and Longitudinal Follow-Up

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Summary

A completed observational study update describing a natural history chart review and longitudinal follow-up for Wolman disease and cholesterol ester storage dis…

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Diseases / indications

• Acid Cholesteryl Ester Hydrolase Deficiency Type 2
• Cholesterol Ester Storage Disease
• Wolman Disease

Snippet

Sponsor: Children's Hospital Medical Center, Cincinnati | Conditions: Wolman Disease, Cholesterol Ester Storage Disease | Status: COMPLETED