Clinical Trial Update: Safety and Efficacy of Recombinant Human Acid Alpha-Glucosidase in the Treatment of Classical Infantile Pompe Disease [Phase 2]

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Summary

Phase 2 clinical trial assessing the safety and efficacy of recombinant human acid alpha-glucosidase for classical infantile Pompe disease; the study has comple…

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Diseases / indications

• Glycogen Storage Disease Type Ii
• Pompe Disease

Drugs mentioned

• Alglucosidase alfa (alglucosidase alfa)

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Pompe Disease, Glycogen Storage Disease Type II | Phase 2 | Status: COMPLETED