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CLINICAL_TRIALS trial_result · 2015-01-21

Clinical Trial Update: Anaplerotic Therapy in Propionic Acidemia [Phase 1]

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Summary

A Phase 1 study evaluating anaplerotic therapy for propionic acidemia has completed.

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Diseases / indications

Snippet

Sponsor: Nicola Longo | Conditions: Propionic Acidemia | Phase 1 | Status: COMPLETED