CLINICAL_TRIALS
other
· 2014-04-02
Clinical Trial Update: BMN 110 US Expanded Access Program
Summary
Expanded access program update for BMN 110 (elosulfase alfa) in Morquio A Syndrome (MPS IVA); status indicates marketing approval.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: BioMarin Pharmaceutical | Conditions: Mucopolysaccharidosis IVA, Morquio A Syndrome | Status: APPROVED_FOR_MARKETING