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CLINICAL_TRIALS other · 2014-04-02

Clinical Trial Update: BMN 110 US Expanded Access Program

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Summary

Expanded access program update for BMN 110 (elosulfase alfa) in Morquio A Syndrome (MPS IVA); status indicates marketing approval.

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Diseases / indications

Drugs mentioned

  • BMN 110 (elosulfase alfa) (elosulfase alfa)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Mucopolysaccharidosis IVA, Morquio A Syndrome | Status: APPROVED_FOR_MARKETING