CLINICAL_TRIALS
research
· 2024-05-20
Clinical Trial Update: Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)
Summary
Expanded access protocol for patisiran in hereditary transthyretin-mediated amyloidosis has been approved for marketing, enabling broader patient access.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Alnylam Pharmaceuticals | Conditions: TTR-mediated Amyloidosis, Amyloidosis, Hereditary | Status: APPROVED_FOR_MARKETING