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CLINICAL_TRIALS research · 2024-05-20

Clinical Trial Update: Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)

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Summary

Expanded access protocol for patisiran in hereditary transthyretin-mediated amyloidosis has been approved for marketing, enabling broader patient access.

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Diseases / indications

Drugs mentioned

  • Patisiran (patisiran)

Snippet

Sponsor: Alnylam Pharmaceuticals | Conditions: TTR-mediated Amyloidosis, Amyloidosis, Hereditary | Status: APPROVED_FOR_MARKETING