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CLINICAL_TRIALS trial_result · 2014-04-09

Clinical Trial Update: Ph 1 Study of ADI PEG 20 in Pediatric Subjects Who Are Argininosuccinate Synthetase (ASS) Deficient [Phase 1]

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Summary

Phase 1 study of ADI-PEG 20 in pediatric patients with Argininosuccinate Synthetase Deficiency has completed. No efficacy results are provided in the summary.

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Diseases / indications

Drugs mentioned

  • ADI-PEG 20 (pegylated arginine deiminase)

Snippet

Sponsor: Polaris Group | Conditions: Argininosuccinate Synthetase Deficient | Phase 1 | Status: COMPLETED