CLINICAL_TRIALS
trial_result
· 2014-04-09
Clinical Trial Update: Ph 1 Study of ADI PEG 20 in Pediatric Subjects Who Are Argininosuccinate Synthetase (ASS) Deficient [Phase 1]
Summary
Phase 1 study of ADI-PEG 20 in pediatric patients with Argininosuccinate Synthetase Deficiency has completed. No efficacy results are provided in the summary.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Polaris Group | Conditions: Argininosuccinate Synthetase Deficient | Phase 1 | Status: COMPLETED