Single-center, Open-label Study of Safety, Pharmacokinetics and Efficacy of rhGAA in Patients With Late-Onset Pompe Disease

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Record identity and dates

Source

ClinicalTrials.gov

Source record ID

NCT00250939

Title field or adapter rule

protocolSection.identificationModule.officialTitle

Ingested At

2026-04-28T10:35:33.534759+00:00

Published At

2014-02-06T00:00:00+00:00

Record Updated At

2014-02-06

Timestamp Basis

source retrieval time was not retained by the feed adapter

Date limitation

source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions

["Pompe Disease (Late-onset)", "Glycogen Storage Disease Type II (GSD-II)", "Acid Maltase Deficiency Disease", "Glycogenosis 2"]

protocolSection.statusModule.lastUpdatePostDateStruct.date

"2014-02-06"

protocolSection.identificationModule.nctId

"NCT00250939"

protocolSection.identificationModule.officialTitle

"Single-center, Open-label Study of Safety, Pharmacokinetics and Efficacy of rhGAA in Patients With Late-Onset Pompe Disease"

protocolSection.statusModule.overallStatus

"COMPLETED"

protocolSection.designModule.phases

["PHASE2"]

protocolSection.statusModule.resultsFirstPostDateStruct.date

""

Study condition terms

• Pompe Disease (Late-onset) (protocolSection.conditionsModule.conditions)
• Glycogen Storage Disease Type II (GSD-II) (protocolSection.conditionsModule.conditions)
• Acid Maltase Deficiency Disease (protocolSection.conditionsModule.conditions)
• Glycogenosis 2 (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

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