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CLINICAL_TRIALS trial_result · 2014-02-06

Clinical Trial Update: A Study of rhGAA in Patients With Late-Onset Pompe Disease [Phase 2]

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Summary

Phase 2 study of recombinant human acid alpha-glucosidase (rhGAA) in patients with late-onset Pompe disease has completed.

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Diseases / indications

Drugs mentioned

  • Myozyme (alglucosidase alfa)

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Pompe Disease (Late-onset), Glycogen Storage Disease Type II (GSD-II) | Phase 2 | Status: COMPLETED